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February 7, 2022: ProQR and the Usher Syndrome Coalition hosted a webinar about the newly announced clinical trials, “Sirius” and “Celeste,” for individuals with Usher syndrome type 2A (USH2A).
Read My Name is Cinnamon” (forthcoming Hay House 2022) is an adventurous tale of a little boy whose life is nothing short of a roller-coaster ride.
Read Orignal Post here
ProQR Announces Positive Results from Clinical Trial of QR-421a in Usher Syndrome and Plans to Start Pivotal Trials QR-421a demonstrated a concordant benefit in multiple measures of vision, including best corrected visual activity (BCVA), static perimetry, and retinal imaging (OCT)
QR-421a observed to be well tolerated with no serious adverse events reported
Two pivotal Phase 2/3 trials are expected to start by the end of 2021
Management to host a conference call today at 8:15am EDT LEIDEN, Netherlands & CAMBRIDGE, Mass.,
Read Transcript of the presentation during USH2020Connections Week, organized by the Usher Syndrome Coalition.
Watche the video presentation here, with caption or ASL.
Read Retina International Usher Syndrome Special Interest Group
Spring Newsletter – Update on events & news relevant during the COVID-19 pandemic
RI USH SIG
Dominique Sturz (AT), Melissa Chaikof (US), Carol Brill (IRL), Dario Sorgato (IT)
We hope that you are all fine and healthy despite the COVID-19 pandemic.
Read Original article on AP News
QR-421a showed early and encouraging evidence of activity, with 25% of patients showing a benefit across multiple concordant outcome measures and was well tolerated with no serious adverse events — QR-421a is the second ophthalmology program where clinical activity was predicted by translational models, further validating the platform — COVID-19 pandemic expected to impact timelines for the pipeline — ProQR anticipates its cash runway will fund operations into H2 2022
LEIDEN, Netherlands & CAMBRIDGE, Mass.,
Read In the month of August 2019 a very interesting and important research study on the life strategies of people with Usher Syndrome type 2A was published in Sweden.
Read On December 2nd Retina International sent the RI USH SIG Winter Newsletter
We are happy to send you the RI USH SIG Winter Newsletter providing you with an update of the latest and upcoming news relevant for people living with Usher Syndrome and with a resource file on USH subtypes, genetic testing and USH genes.
Read Last September 21st, on the occasion of Global Usher Syndrome Awareness Day, we published the video “Usher Syndrome. Game Over” on our social media channels.
Read 